Abu Dhabi leads world in breakthrough gene replacement therapy 'ITVISMA' for spinal muscular atrophy

Dec 28, 2025

Abu Dhabi has become the first place globally to deliver ITVISMA gene therapy for spinal muscular atrophy, marking a major healthcare milestone and reinforcing...

UAE approves gene replacement therapy for new age group in spinal muscular atrophy patients

Dec 20, 2025

The Emirates Drug Establishment (EDE) has announced the approval of Itvisma (onasemnogene abeparvovec), a gene therapy that uses an adeno-associated viral vector to treat...